The UK regulatory authorities have approved the first ever trial of a revolutionary gene therapy for young children diagnosed with Hunter syndrome, a devastating rare lysosomal storage disorder.
ITV Tyne Tees and Granada Reports recently featured the journey of two-year-old Teddi Shaw, who became the first child in the UK to receive NHS life-saving gene therapy treatment, Libmeldy® at MFT.
A revolutionary ward-based genetic test which can prevent stroke related death has received a UKCA product mark, paving the way for its introduction to the NHS.
An innovative genetic test that can help prevent newborn babies from going deaf if treated with a common antibiotic, is now being used in routine clinical practice in maternity settings at MFT.
Researchers tell an international conference that a new gene therapy for Sanfilippo disease – also known as childhood dementia – has shown promising early results in a proof-of-concept study.