ITV Tyne Tees and Granada Reports recently featured the journey of two-year-old Teddi Shaw, who became the first child in the UK to receive NHS life-saving gene therapy treatment, Libmeldy® at MFT.
For a nine-year old boy and his family, being part of Duchenne Muscular Dystrophy clinical research at NIHR Manchester CRF at Royal Manchester Children's Hospital has been ‘amazing,’ for many reasons.
Pioneering research has shown dramatic results for treating children with high-risk leukaemia (a type of blood cancer), who previously had no hope of recovery after all other treatment options failed.
Researchers tell an international conference that a new gene therapy for Sanfilippo disease – also known as childhood dementia – has shown promising early results in a proof-of-concept study.
A 20-month-old baby girl has become the first child in the UK to receive a life-saving gene therapy treatment for the fatal disorder, metachromatic leukodystrophy disease (MLD).
Children with cancer in Greater Manchester and Lancashire could be given new hope after a funding boost for research into experimental cancer treatments.
Parents across Greater Manchester, East Lancashire and East Cheshire are being urged to support a new respiratory virus study looking into the UK’s leading cause of infant hospitalisation.